Emicizumab

Emicizumab
Monoclonal antibody
TypeWhole antibody
SourceHumanized
TargetActivated factor IX, factor X
Clinical data
Trade namesHemlibra
Other namesACE910, RG6013, emicizumab-kxwh
AHFS/Drugs.comMonograph
MedlinePlusa622046
License data
Pregnancy
category
Routes of
administration
Subcutaneous
ATC code
Legal status
Legal status
Identifiers
CAS Number
DrugBank
ChemSpider
  • none
UNII
KEGG
Chemical and physical data
FormulaC6434H9940N1724O2047S45
Molar mass145639.02 g·mol−1


Emicizumab, sold under the brand name Hemlibra, is a humanized bispecific monoclonal antibody for the treatment of haemophilia A, developed by Genentech and Chugai (both organizations are subsidiaries of Hoffmann-La Roche).[4] Emicizumab is a bispecific factor IXa- and factor X-directed antibody.[3]

In November 2017, it was approved in the United States for treatment of haemophilia A in those who had developed resistance to other treatments.[5] It was subsequently approved by the US FDA in April 2018, under the breakthrough therapy designation for the treatment of haemophila A in those who have not developed resistance to other treatments.[6] The U.S. Food and Drug Administration (FDA) considers it to be a first-in-class medication.[7]

  1. ^ a b "AUSTRALIAN PRODUCT INFORMATION – Hemlibra (Emicizumab)". Archived from the original on 15 May 2023. Retrieved 8 January 2023.
  2. ^ "Summary Basis of Decision (SBD) for Hemlibra". Health Canada. 23 October 2014. Retrieved 29 May 2022.
  3. ^ a b "Hemlibra- emicizumab injection, solution". DailyMed. 28 October 2024. Retrieved 11 July 2025.
  4. ^ Spreitzer H (4 July 2016). "Neue Wirkstoffe - Emicizumab". Österreichische Apothekerzeitung (in German) (14/2016).
  5. ^ "Roche hemophilia drug wins FDA nod, with a warning". Reuters. 17 November 2017.
  6. ^ "FDA Grants Roche Breakthrough Therapy Designation on Hemophilia Drug". BioPharm International. UBM. 19 April 2018. Retrieved 20 April 2018.
  7. ^ New Drug Therapy Approvals 2017. U.S. Food and Drug Administration (FDA) (Report). January 2018. Archived from the original (PDF) on 14 September 2019. Retrieved 16 September 2020.